EP 1025251 A1 20000809 - AMPLIFIABLE ADENO-ASSOCIATED VIRUS (AAV) PACKAGING CASSETTES FOR THE PRODUCTION OF RECOMBINANT AAV VECTORS
Title (en)
AMPLIFIABLE ADENO-ASSOCIATED VIRUS (AAV) PACKAGING CASSETTES FOR THE PRODUCTION OF RECOMBINANT AAV VECTORS
Title (de)
VERMEHRBARE 'VERPACKUNGS-KASSETTEN' DES ADENO-ASSOZIIERTEN VIRUS (AAV) FÜR DIE PRODUKTION VON REKOMBINANTEN AAV-VEKTOREN
Title (fr)
CASSETTES D'ENCAPSIDATION DE VIRUS ADENO-ASSOCIE (AAV) AMPLIFIABLE POUR LA PRODUCTION DE VECTEURS DE AAV RECOMBINES
Publication
Application
Priority
- US 9821938 W 19981020
- US 95523297 A 19971021
Abstract (en)
[origin: WO9920779A1] High-efficiency AAV packaging constructs and methods for their use are provided in the present invention. These high-efficiency packaging constructs comprise an activating element (such as the P1 sequence located within the AAV S1 integration site of human chromosome 19) amplifiably linked to one or more AAV packaging genes. The constructs may be either integrated into a mammalian cell genome or maintained episomally. Use of the high-efficiency AAV packaging vectors of the invention provides for controlled amplifiable production of rAAV vector constructs.
IPC 1-7
IPC 8 full level
C12N 7/00 (2006.01); C12N 7/01 (2006.01); C12N 15/09 (2006.01); C12N 15/864 (2006.01)
CPC (source: EP)
C12N 7/00 (2013.01); C12N 15/86 (2013.01); C12N 2750/14143 (2013.01); C12N 2750/14152 (2013.01)
Citation (search report)
See references of WO 9920779A1
Designated contracting state (EPC)
AT BE CH CY DE DK ES FI FR GB GR IE IT LI LU MC NL PT SE
DOCDB simple family (publication)
WO 9920779 A1 19990429; AU 1096799 A 19990510; AU 758541 B2 20030327; CA 2308008 A1 19990429; EP 1025251 A1 20000809; JP 2001520051 A 20011030
DOCDB simple family (application)
US 9821938 W 19981020; AU 1096799 A 19981020; CA 2308008 A 19981020; EP 98953640 A 19981020; JP 2000517099 A 19981020