EP 2804600 A4 20150902 - METHODS AND FORMULATIONS FOR TREATING SIALIC ACID DEFICIENCIES
Title (en)
METHODS AND FORMULATIONS FOR TREATING SIALIC ACID DEFICIENCIES
Title (de)
VERFAHREN UND FORMULIERUNGEN ZUR BEHANDLUNG VON SIALINSÄUREMANGEL
Title (fr)
PROCÉDÉS ET FORMULATIONS PERMETTANT DE TRAITER LES DÉFICIENCES EN ACIDE SIALIQUE
Publication
Application
Priority
- US 201261588069 P 20120118
- US 201261709549 P 20121004
- US 2013022167 W 20130118
Abstract (en)
[origin: CN104271125A] The invention relates to an oral formulation for treating sialic acid deficiencies, which comprises sialic acid of an effective dose, or pharmaceutically acceptable salt, solvate or ester.
IPC 8 full level
A61K 31/7012 (2006.01); A61K 9/20 (2006.01); A61K 9/22 (2006.01); A61P 21/00 (2006.01)
CPC (source: CN EP)
A61K 9/0002 (2013.01 - CN); A61K 9/205 (2013.01 - CN EP); A61K 9/2054 (2013.01 - CN EP); A61K 31/7012 (2013.01 - CN EP); A61P 21/00 (2017.12 - EP)
Citation (search report)
- [XP] WO 2012009474 A1 20120119 - ULTRAGENYX PHARMACEUTICAL INC [US], et al
- [E] WO 2013063149 A1 20130502 - ULTRAGENYX PHARMACEUTICAL INC [US]
- [Y] WO 2008150477 A2 20081211 - US GOV HEALTH & HUMAN SERV [US], et al
- [Y] WO 2010131712 A1 20101118 - JAPAN HEALTH SCIENCE FOUND [JP], et al & US 2012264928 A1 20121018 - NOGUCHI SATORU [JP], et al
- [Y] US 2010159001 A1 20100624 - CARDINAL JOHN R [US], et al
- [Y] MAY CHRISTINE V MALICDAN ET AL: "Prophylactic treatment with sialic acid metabolites precludes the development of the myopathic phenotype in the DMRV-hIBM mouse model", NATURE MEDICINE, vol. 15, no. 6, 1 June 2009 (2009-06-01), pages 690 - 695, XP055175431, ISSN: 1078-8956, DOI: 10.1038/nm.1956
- See references of WO 2013109906A2
Designated contracting state (EPC)
AL AT BE BG CH CY CZ DE DK EE ES FI FR GB GR HR HU IE IS IT LI LT LU LV MC MK MT NL NO PL PT RO RS SE SI SK SM TR
DOCDB simple family (publication)
WO 2013109906 A2 20130725; AU 2013209610 A1 20140710; AU 2013209610 B2 20171130; BR 112014017587 A2 20170613; BR 112014017587 A8 20170704; CA 2862836 A1 20130725; CN 104271125 A 20150107; EP 2804600 A2 20141126; EP 2804600 A4 20150902; IL 233225 A0 20140831; JP 2015504094 A 20150205; JP 2017186381 A 20171012; KR 20150000872 A 20150105
DOCDB simple family (application)
US 2013022167 W 20130118; AU 2013209610 A 20130118; BR 112014017587 A 20130118; CA 2862836 A 20130118; CN 201380015020 A 20130118; EP 13739040 A 20130118; IL 23322514 A 20140618; JP 2014553457 A 20130118; JP 2017141883 A 20170721; KR 20147022912 A 20130118