EP 3389671 A1 20181024 - ANTISENSE OLIGOMERS FOR TREATMENT OF ALAGILLE SYNDROME
Title (en)
ANTISENSE OLIGOMERS FOR TREATMENT OF ALAGILLE SYNDROME
Title (de)
ANTISENSE-OLIGOMERE ZUR BEHANDLUNG DES ALAGILLE-SYNDROMS
Title (fr)
OLIGOMÈRES ANTISENS POUR LE TRAITEMENT DU SYNDROME D'ALAGILLE
Publication
Application
Priority
- US 201562267210 P 20151214
- US 2016066414 W 20161213
Abstract (en)
[origin: WO2017106210A1] Provided herein are methods and compositions for increasing the expression of JAGl, and for treating a subject in need thereof, e.g., a subject with deficient JAGl protein expression or a subject having Alagille syndrome (ALGS).
IPC 8 full level
A61K 31/7088 (2006.01); C12N 15/11 (2006.01); C12N 15/113 (2010.01); C12Q 1/68 (2018.01)
CPC (source: EP)
A61K 31/7088 (2013.01); A61P 1/16 (2018.01); A61P 21/04 (2018.01); A61P 43/00 (2018.01); C12N 15/111 (2013.01); C12N 15/113 (2013.01); C12Q 1/68 (2013.01); C12Q 1/6883 (2013.01); C12N 2310/11 (2013.01); C12N 2310/315 (2013.01); C12N 2310/321 (2013.01); C12N 2320/33 (2013.01); C12Q 2600/156 (2013.01)
C-Set (source: EP)
Designated contracting state (EPC)
AL AT BE BG CH CY CZ DE DK EE ES FI FR GB GR HR HU IE IS IT LI LT LU LV MC MK MT NL NO PL PT RO RS SE SI SK SM TR
Designated extension state (EPC)
BA ME
DOCDB simple family (publication)
WO 2017106210 A1 20170622; CA 3005245 A1 20170622; EP 3389671 A1 20181024; EP 3389671 A4 20190717; JP 2018538288 A 20181227; JP 2022106803 A 20220720
DOCDB simple family (application)
US 2016066414 W 20161213; CA 3005245 A 20161213; EP 16876499 A 20161213; JP 2018529221 A 20161213; JP 2022069164 A 20220420