EP 3390635 A1 20181024 - ANTISENSE OLIGOMERS FOR TREATMENT OF TUBEROUS SCLEROSIS COMPLEX
Title (en)
ANTISENSE OLIGOMERS FOR TREATMENT OF TUBEROUS SCLEROSIS COMPLEX
Title (de)
ANTISENSE-OLIGOMERE ZUR BEHANDLUNG EINES TUBERÖSEN SKLEROSEKOMPLEXES
Title (fr)
OLIGOMÈRES ANTISENS POUR LE TRAITEMENT DE LA SCLÉROSE TUBÉREUSE DE BOURNEVILLE
Publication
Application
Priority
- US 201562267212 P 20151214
- US 2016066705 W 20161214
Abstract (en)
[origin: WO2017106375A1] Provided herein are methods and compositions for increasing the expression of TSC2, and for treating a subject in need thereof, such as a subject with deficient tuberin protein expression or a subject having tuberous sclerosis complex.
IPC 8 full level
C12N 15/113 (2010.01); C12Q 1/68 (2018.01)
CPC (source: EP)
A61K 31/7088 (2013.01); A61P 13/12 (2017.12); A61P 25/00 (2017.12); A61P 35/00 (2017.12); C12N 15/1135 (2013.01); C12Q 1/6883 (2013.01); C12N 2310/11 (2013.01); C12Q 2600/156 (2013.01); C12Q 2600/178 (2013.01)
Designated contracting state (EPC)
AL AT BE BG CH CY CZ DE DK EE ES FI FR GB GR HR HU IE IS IT LI LT LU LV MC MK MT NL NO PL PT RO RS SE SI SK SM TR
Designated extension state (EPC)
BA ME
DOCDB simple family (publication)
WO 2017106375 A1 20170622; CA 3005131 A1 20170622; EP 3390635 A1 20181024; EP 3390635 A4 20190501; JP 2019500350 A 20190110; JP 2022088533 A 20220614; JP 7051683 B2 20220411
DOCDB simple family (application)
US 2016066705 W 20161214; CA 3005131 A 20161214; EP 16876615 A 20161214; JP 2018529258 A 20161214; JP 2022053948 A 20220329