Global Patent Index - EP 3846780 A4

EP 3846780 A4 20221130 - ENZYMATIC ASSAYS FOR QUANTIFYING THERAPY IN SUBJECTS WITH MUCOPOLYSACCHARIDOSIS TYPE I OR II

Title (en)

ENZYMATIC ASSAYS FOR QUANTIFYING THERAPY IN SUBJECTS WITH MUCOPOLYSACCHARIDOSIS TYPE I OR II

Title (de)

ENZYMATISCHE TESTS ZUR QUANTIFIZIERUNG DER THERAPIE BEI PATIENTEN MIT MUCOPOLYSACCHARIDOSE TYP I ODER II

Title (fr)

DOSAGES ENZYMATIQUES POUR QUANTIFIER UNE THÉRAPIE CHEZ DES SUJETS ATTEINTS DE MUCOPOLYSACCHARIDOSE DE TYPE I OU II

Publication

EP 3846780 A4 20221130 (EN)

Application

EP 19857764 A 20190807

Priority

  • US 201962801110 P 20190206
  • US 201962802104 P 20190206
  • US 201862727465 P 20180905
  • US 201962802558 P 20190207
  • US 201962802568 P 20190207
  • US 201962812592 P 20190301
  • US 2019045491 W 20190807

Abstract (en)

[origin: WO2020050947A2] Described herein are enzymatic assays for assessing in vivo therapy of MPSII (Hunter) or MPSI (Hurler) subjects.

IPC 8 full level

A61K 9/00 (2006.01); A61K 38/46 (2006.01); A61K 47/42 (2017.01); C12N 9/16 (2006.01); C12N 9/24 (2006.01); C12N 9/40 (2006.01)

CPC (source: EP)

C12N 9/16 (2013.01); C12N 9/2402 (2013.01); C12Q 1/44 (2013.01); C12Y 301/06013 (2013.01); C12Y 302/01076 (2013.01)

Citation (search report)

  • [A] WO 2016100603 A1 20160623 - SHIRE HUMAN GENETIC THERAPIES [US]
  • [X] "JIMD Reports - Volume 11", vol. 38, 1 January 2017, SPRINGER BERLIN HEIDELBERG, Berlin, Heidelberg, ISBN: 978-3-642-37328-2, ISSN: 2192-8304, article AZADEH MITRA ET AL: "A Rapid Two-Step Iduronate-2-Sulfatatse Enzymatic Activity Assay for MPSII Pharmacokinetic Assessment", pages: 89 - 95, XP055970626, DOI: 10.1007/8904_2017_34
  • See references of WO 2020050947A2

Designated contracting state (EPC)

AL AT BE BG CH CY CZ DE DK EE ES FI FR GB GR HR HU IE IS IT LI LT LU LV MC MK MT NL NO PL PT RO RS SE SI SK SM TR

DOCDB simple family (publication)

WO 2020050947 A2 20200312; WO 2020050947 A3 20200723; EP 3846780 A2 20210714; EP 3846780 A4 20221130; JP 2022512542 A 20220207

DOCDB simple family (application)

US 2019045491 W 20190807; EP 19857764 A 20190807; JP 2021512419 A 20190807