EP 4106801 A1 20221228 - COMPOUND FOR THE TREATMENT OF A GLYCOGENOSIS
Title (en)
COMPOUND FOR THE TREATMENT OF A GLYCOGENOSIS
Title (de)
VERBINDUNG ZUR BEHANDLUNG EINER GLYKOGENOSE
Title (fr)
COMPOSÉ DE TRAITEMENT DE GLYCOGÉNOSE
Publication
Application
Priority
- IT 202000003371 A 20200219
- IB 2021051322 W 20210217
Abstract (en)
[origin: WO2021165841A1] The present invention relates to a compound selected from a polynucleotide coding for a glycogen debranching enzyme (GDE), a vector and a host cell comprising the polynucleotide. The present invention further relates to the use of the compound for the treatment of a glycogenosis (GSD), preferably GSDIII.
IPC 8 full level
A61K 38/47 (2006.01); C12N 9/10 (2006.01); C12N 9/24 (2006.01)
CPC (source: EP)
C12N 9/1051 (2013.01); C12N 9/2402 (2013.01); A61K 38/00 (2013.01)
Citation (search report)
See references of WO 2021165841A1
Designated contracting state (EPC)
AL AT BE BG CH CY CZ DE DK EE ES FI FR GB GR HR HU IE IS IT LI LT LU LV MC MK MT NL NO PL PT RO RS SE SI SK SM TR
Designated extension state (EPC)
BA ME
Designated validation state (EPC)
KH MA MD TN
DOCDB simple family (publication)
WO 2021165841 A1 20210826; EP 4106801 A1 20221228; IT 202000003371 A1 20210819
DOCDB simple family (application)
IB 2021051322 W 20210217; EP 21712896 A 20210217; IT 202000003371 A 20200219