EP 4308172 A2 20240124 - GENE THERAPY COMPOSITION AND TREATMENT OF RIGHT VENTRICULAR ARRHYTHMOGENIC CARDIOMYOPATHY
Title (en)
GENE THERAPY COMPOSITION AND TREATMENT OF RIGHT VENTRICULAR ARRHYTHMOGENIC CARDIOMYOPATHY
Title (de)
GENTHERAPIEZUSAMMENSETZUNG UND BEHANDLUNG VON RECHTSVENTRIKULÄRER ARRHYTHMOGENER KARDIOMYOPATHIE
Title (fr)
COMPOSITION DE THÉRAPIE GÉNIQUE ET TRAITEMENT DE LA CARDIOMYOPATHIE ARYTHMOGÈNE VENTRICULAIRE DROITE
Publication
Application
Priority
- US 202163163393 P 20210319
- EP 2022057145 W 20220318
Abstract (en)
[origin: WO2022195074A2] Disclosed are a composition and method of treating or preventing cardiomyopathy in a human subject. In some embodiments, the method comprises delivering a therapeutic dose of a gene therapy vector to cardiomyocytes of the human subject, wherein the gene therapy vector comprises a nucleic acid sequence encoding for PKP2.
IPC 8 full level
A61K 48/00 (2006.01); C12N 15/86 (2006.01)
CPC (source: EP IL KR US)
A61K 38/1709 (2013.01 - US); A61K 48/0041 (2013.01 - US); A61K 48/005 (2013.01 - EP IL KR); A61K 48/0058 (2013.01 - EP IL KR US); A61P 9/04 (2018.01 - KR US); A61P 9/10 (2018.01 - KR); C07K 14/47 (2013.01 - EP IL KR); C07K 14/4716 (2013.01 - EP IL KR); C12N 15/86 (2013.01 - EP IL KR US); C12N 2750/14143 (2013.01 - EP IL KR US); C12N 2750/14145 (2013.01 - US)
Designated contracting state (EPC)
AL AT BE BG CH CY CZ DE DK EE ES FI FR GB GR HR HU IE IS IT LI LT LU LV MC MK MT NL NO PL PT RO RS SE SI SK SM TR
Designated extension state (EPC)
BA ME
Designated validation state (EPC)
KH MA MD TN
DOCDB simple family (publication)
WO 2022195074 A2 20220922; WO 2022195074 A3 20221110; AU 2022239846 A1 20231026; AU 2022239846 A9 20231109; BR 112023018944 A2 20231226; CA 3212043 A1 20220922; CN 117715660 A 20240315; EP 4308172 A2 20240124; IL 305959 A 20231101; JP 2024512483 A 20240319; KR 20230159471 A 20231121; TW 202300180 A 20230101; US 2024042059 A1 20240208
DOCDB simple family (application)
EP 2022057145 W 20220318; AU 2022239846 A 20220318; BR 112023018944 A 20220318; CA 3212043 A 20220318; CN 202280034403 A 20220318; EP 22718072 A 20220318; IL 30595923 A 20230914; JP 2023557131 A 20220318; KR 20237034942 A 20220318; TW 111110077 A 20220318; US 202218282061 A 20220318