EP 4373939 A2 20240529 - GENOME EDITING COMPOSITIONS AND METHODS FOR TREATMENT OF CHRONIC GRANULOMATOUS DISEASE
Title (en)
GENOME EDITING COMPOSITIONS AND METHODS FOR TREATMENT OF CHRONIC GRANULOMATOUS DISEASE
Title (de)
GENOMEDITIERUNGSZUSAMMENSETZUNGEN UND VERFAHREN ZUR BEHANDLUNG VON CHRONISCHER GRANULOMATÖSER ERKRANKUNG
Title (fr)
COMPOSITIONS D'ÉDITION DE GÉNOME ET MÉTHODES DE TRAITEMENT DE MALADIE GRANULOMATEUSE CHRONIQUE
Publication
Application
Priority
- US 202163225100 P 20210723
- US 2022074088 W 20220723
Abstract (en)
[origin: WO2023004439A2] Provided herein are compositions and methods of using prime editing systems comprising prime editors and prime editing guide RNAs for treatment of genetic disorders.
IPC 8 full level
C12N 15/113 (2010.01); A61K 35/28 (2015.01); A61K 38/46 (2006.01); C12N 5/10 (2006.01)
CPC (source: EP US)
A61P 37/02 (2018.01 - US); C12N 9/22 (2013.01 - US); C12N 15/102 (2013.01 - US); C12N 15/1137 (2013.01 - EP); C12N 15/907 (2013.01 - EP); C12N 2310/20 (2017.05 - EP US); C12N 2320/34 (2013.01 - EP); C12Y 106/03001 (2013.01 - EP)
Designated contracting state (EPC)
AL AT BE BG CH CY CZ DE DK EE ES FI FR GB GR HR HU IE IS IT LI LT LU LV MC MK MT NL NO PL PT RO RS SE SI SK SM TR
Designated extension state (EPC)
BA ME
Designated validation state (EPC)
KH MA MD TN
DOCDB simple family (publication)
WO 2023004439 A2 20230126; WO 2023004439 A3 20230302; EP 4373939 A2 20240529; US 2024011007 A1 20240111
DOCDB simple family (application)
US 2022074088 W 20220723; EP 22846874 A 20220723; US 202318449230 A 20230814