(19)
(11)EP 3 758 714 A1

(12)

(43)Date of publication:
06.01.2021 Bulletin 2021/01

(21)Application number: 19761013.2

(22)Date of filing:  27.02.2019
(51)International Patent Classification (IPC): 
A61K 31/7088(2006.01)
C12N 15/63(2006.01)
C12N 15/113(2010.01)
A61P 25/00(2006.01)
(86)International application number:
PCT/US2019/019789
(87)International publication number:
WO 2019/168950 (06.09.2019 Gazette  2019/36)
(84)Designated Contracting States:
AL AT BE BG CH CY CZ DE DK EE ES FI FR GB GR HR HU IE IS IT LI LT LU LV MC MK MT NL NO PL PT RO RS SE SI SK SM TR
Designated Extension States:
BA ME
Designated Validation States:
KH MA MD TN

(30)Priority: 27.02.2018 US 201862635815 P

(71)Applicant: The University of North Carolina at Chapel Hill
Chapel Hill, North Carolina 27516 (US)

(72)Inventors:
  • ZYLKA, Mark John
    Chapel Hill, North Carolina 27516 (US)
  • WOLTER, Justin Matthew
    Pittsboro, North Carolina 27312 (US)
  • FRAGOLA, Giulia
    Durham, North Carolina 27707 (US)
  • SIMON, Jeremy Mark
    Carrboro, North Carolina 27510 (US)
  • MAO, Hanqian
    Durham, North Carolina 27705 (US)

(74)Representative: HGF 
1 City Walk
Leeds LS11 9DX
Leeds LS11 9DX (GB)

  


(54)METHODS AND COMPOSITIONS FOR TREATING ANGELMAN SYNDROME