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WO9807859A   [0088] 
WO9809985A   [0089] 

Nature Biotechnology   [0028] 
Molecular Cloning: A Laboratory Manual   [0070] 
Current Protocols in Molecular Biology   [0070] 
DNA Isolation and Sequencing: Essential Techniques   [0070] 
In Situ Hybridization: Principles and Practice   [0070] 
Oligonucleotide Synthesis: A Practical Approach   [0070] 
Methods of Enzymology: DNA Structure Part A: Synthesis and Physical Analysis of DNA Methods in Enzymology   [0070] 
Using Antibodies : A Laboratory Manual : Portable Protocol NO. I   [0070] 
Antibodies : A Laboratory Manual   [0070] 
Handbook of Drug Screening   [0070] 
Lab Ref: A Handbook of Recipes, Reagents, and Other Reference Tools for Use at the Bench   [0070] 
Efficient retrovirus-mediated transfer of the multidrug resistance 1 gene into autologous human long-term rep opulating hematopoietic stem cells   [0157] 
A clonogenic common myeloid progenitor that gives rise to all myeloid lineages   [0157] 
Coordinate dual-gene transgenesis by lentiviral vectors carrying synthetic bidirectional promoters   [0157] 
Isolation and characterization of immature oligodendrocyte lineage cells   [0157] 
Modeling the initiation and progression of human acute leukemia in mice   [0157] 
MicroRNAs: genomics, biogenesis, mechanism, and function   [0157] 
MicroRNAs: target recognition and regulatory functions   [0157] 
Regulation by sphingosine 1-phosphate of Bax and Bad activities during apoptosis in a MEK-dependent manner   [0157] 
Gene therapy of metachromatic leukodystrophy reverses neurological damage and deficits in mice   [0157] 
Correction of metachromatic leukodystrophy in the mouse model by transplantation of genetically modified hematopoietic stem cells   [0157] 
Correction of Metachromatic Leukodystrophy in the Mouse Model by Transplantation of Genetically Modified Hematopoietic Stem Cells   [0157] 
Myelin glycosphingolipids, galactosylceramide and sulfatide, participate in carbohydrate-carbohydrate interactions between apposed membranes and may form glycosynapses between oligodendrocyte and/or myelin membranes   [0157] 
Enzyme-replacement therapy for metabolic storage disorders   [0157] 
Enzyme replacement for lysosomal diseases   [0157] 
Principles of microRNA-target recognition   [0157] 
Induction of intracellular ceramide by interleukin-1 beta in oligodendrocytes   [0157] 
A microRNA -regulated lentiviral vector mediates stable correction of hemophilia B mice   [0157] 
Endogenous microRNA can be broadly exploited to regulate transgene expression according to tissue, lineage and differentiation state   [0157] 
Endogenous microRNA regulation suppresses transgene expression in hematopoietic lineages and enables stable gene transfer   [0157] 
Safety of Arylsulfatase A Overexpression for Gene Therapy of Metachromatic Leukodystrophy   [0157] 
MicroRNAs modulate hematopoietic lineage differentiation   [0157] 
Integrin-associated Lyn kinase promotes cell survival by suppressing acid sphingomyelinase activity   [0157] 
The emerging role of microRNAs in cardiac remodeling and heart failure   [0157] 
A minicircuitry comprised of microRNA-223 and transcription factors NFI-A and C/EBPalpha regulates human granulopoiesis   [0157] 
miR-126 regulates angiogenic signaling and vascular integrity   [0157] 
Stem cell transplantation and gene therapy for hemoglobinopathies   [0157] 
Stable knockdown of microRNA in vivo by lentiviral vectors   [0157] 
Stable knockdown of microRNA in vivo by lentiviral vectors   [0157] 
Multipotential stem cells from the adult mouse brain proliferate and self-renew in response to basic fibroblast growth factor   [0157] 
Kinetic analysis of the RNAi enzyme complex   [0157] 
Sphingosine-1 -phosphate induces proliferation and morphological changes of neural progenitor cells   [0157] 
microRNAs join the p53 network--another piece in the tumour-suppression puzzle   [0157] 
Human CD34+ hematopoietic progenitor cell-directed lentiviral-mediated gene therapy in a xenotransplantation model of lysosomal storage disease   [0157] 
Elevation of the level and activity of acid ceramidase in Alzheimer's disease brain   [0157] 
Oxidative stress kills human primary oligodendrocytes via neutral sphingomyelinase: implications for multiple sclerosis   [0157] 
Regulation of progenitor cell proliferation and granulocyte function by microRNA -223   [0157] 
Tumor growth need not be driven by rare cancer stem cells   [0157] 
SLAM family receptors distinguish hematopoietic stem and progenitor cells and reveal endothelial niches for stem cells   [0157] 
Destabilized green fluorescent protein detects rapid removal of transcription blocks after genotoxic exposure   [0157] 
Silencing of microRNAs in vivo with 'antagomirs   [0157] 
MicroRNAs: a new class of regulatory genes affecting metabolism   [0157] 
Role of Dicer and Drosha for endothelial microRNA expression and angiogenesis   [0157] 
New microRNAs from mouse and human   [0157] 
A mammalian microRNA expression atlas based on small RNA library sequencing   [0157] 
Amyloid-beta peptide induces oligodendrocyte death by activating the neutral sphingomyelinase-ceramide pathway   [0157] 
The C. elegans heterochronic gene lin-4 encodes small RNAs with antisense complementarity to lin-14   [0157] 
Nuclear export of microRNA precursors   [0157] 
Sphingosine 1-phosp hate phosphatase 2 is induced during inflammatory responses   [0157] 
Long non-coding RNAs: insights into functions   [0157] 
In vivo gene delivery and stable transduction of nondividing cells by a lentiviral vector   [0157] 
Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1 -EVI1, PRDM1 6 or SETBP1   [0157] 
Advances in the treatment of Chronic Granulomatous Disease by gene therapy   [0157] 
MicroRNA function: multiple mechanisms for a tiny RNA?   [0157] 
Elucidation of the phenotypic, functional, and molecular topography of a myeloerythroid progenitor cell hierarchy   [0157] 
The 21-nucleotide let-7 RNA regulates developmental timing in Caenorhabditis elegans   [0157] 
The alliance of sphingosine-1 -phosphate and its receptors in immunity   [0157] 
Treatment of lysosomal storage disorders : progress with enzyme replacement therapy   [0157]  [0157] 
The interplay between the master transcription factor PU.1 and miR-424 regulates human monocyte/macrophage differentiation   [0157] 
Progress toward the genetic treatment of the beta-thalassemias   [0157] 
Recent advances in globin gene transfer for the treatment of beta-thalassemia and sickle cell anemia   [0157] 
Murine mucopolysaccharidosis type VII: long term therapeutic effects of enzyme replacement and enzyme replacement followed by bone marrow transplantation   [0157] 
Chemokine-induced recruitment of genetically modified bone marrow cells into the CNS of GM1-gangliosidosis mice corrects neuronal pathology   [0157] 
Asymmetry in the assembly of the RNAi enzyme complex   [0157] 
Differential responses of oligodendrocytes to tumor necrosis factor and other pro-apoptotic agents: role of ceramide in apoptosis   [0157] 
Sequential generations of hematopoietic colonies derived from single nonlineage-committed CD34+ CD38- progenitor cells   [0157] 
Perspective: machines for RNAi   [0157] 
The endothelial-specific microRNA miR-126 governs vascular integrity and angiogenesis   [0157] 
Genetic correction of p67phox deficient chronic granulomatous disease using peripheral blood progenitor cells as a target for ret rovirus mediated gene transfer   [0157] 
Gene therapy: therapeutic gene causing lymphoma   [0157] 
Infiltration of hematogenous lineage cells into the demyelinating central nervous system of twitcher mice   [0157] 
MicroRNA control in the immune system: basic principles   [0157] 
Prolonged survival and remyelination after hematopoietic cell transplantation in the twitcher mouse   [0157] 
Hematopoietic cell transplantation in the twitcher mouse. The effects of pretransplant conditioning with graded doses of busulfan   [0157] 
Stem cell transplantation in hemoglobinopathies   [0157] 
Exportin-5 mediates the nuclear export of premicroRNAs and short hairpin RNAs   [0157]