(19)
(11) EP 3 691 656 A1

(12)

(43) Date of publication:
12.08.2020 Bulletin 2020/33

(21) Application number: 18797262.5

(22) Date of filing: 09.10.2018
(51) International Patent Classification (IPC): 
A61K 31/713(2006.01)
A61K 31/395(2006.01)
A61K 31/4418(2006.01)
A61K 31/519(2006.01)
A61K 31/5377(2006.01)
A61P 3/00(2006.01)
A61K 31/4375(2006.01)
A61K 31/506(2006.01)
A61K 31/52(2006.01)
A61K 31/5513(2006.01)
(86) International application number:
PCT/US2018/055087
(87) International publication number:
WO 2019/071276 (11.04.2019 Gazette 2019/15)
(84) Designated Contracting States:
AL AT BE BG CH CY CZ DE DK EE ES FI FR GB GR HR HU IE IS IT LI LT LU LV MC MK MT NL NO PL PT RO RS SE SI SK SM TR
Designated Extension States:
BA ME
Designated Validation States:
KH MA MD TN

(30) Priority: 06.10.2017 US 201762568893 P

(71) Applicant: Camp4 Therapeutics Corporation
Cambridge, MA 02139 (US)

(72) Inventors:
  • SEHGAL, Alfica
    Cambridge MA 02139 (US)
  • SIGOVA, Alla, A.
    Cambridge MA 02139 (US)
  • ZLOBINE, Igor
    Cambridge MA 02139 (US)
  • SCHWARTZ, Brian, E.
    Cambridge MA 02139 (US)
  • BUMCROT, David, A.
    Cambridge MA 02139 (US)

(74) Representative: Elkington and Fife LLP 
Prospect House 8 Pembroke Road
Sevenoaks, Kent TN13 1XR
Sevenoaks, Kent TN13 1XR (GB)

   


(54) METHODS AND COMPOSITIONS FOR TREATING UREA CYCLE DISORDERS, IN PARTICULAR OTC DEFICIENCY