(19)
(11) EP 3 775 212 A1

(12)

(43) Date of publication:
17.02.2021 Bulletin 2021/07

(21) Application number: 19722955.2

(22) Date of filing: 05.04.2019
(51) International Patent Classification (IPC): 
C12N 15/113(2010.01)
(86) International application number:
PCT/IB2019/052820
(87) International publication number:
WO 2019/197954 (17.10.2019 Gazette 2019/42)
(84) Designated Contracting States:
AL AT BE BG CH CY CZ DE DK EE ES FI FR GB GR HR HU IE IS IT LI LT LU LV MC MK MT NL NO PL PT RO RS SE SI SK SM TR
Designated Extension States:
BA ME
Designated Validation States:
KH MA MD TN

(30) Priority: 10.04.2018 IT 201800004359

(71) Applicants:
  • Universita' Cattolica Del Sacro Cuore
    20123 Milano Mi (IT)
  • Università degli Studi di Roma "La Sapienza"
    00185 Roma (IT)
  • Fondazione Istituto Italiano di Tecnologia
    16163 Genova (IT)

(72) Inventors:
  • TIZIANO, Francesco Danilo
    00168 Roma (RM) (IT)
  • INFANTE, Paola
    00167 Roma (IT)
  • DI MARCOTULLIO, Lucia
    00187 Roma (IT)
  • ABIUSI, Emanuela
    00168 Roma (IT)

(74) Representative: Di Giovine, Paolo et al
Società Italiana Brevetti S.p.A. Piazza di Pietra, 38-39
00186 Roma
00186 Roma (IT)

   


(54) IDENTIFICATION OF MUSCULAR MIRNAS AS MOLECULAR BIOMARKERS AND CO-ADJUVANT FOR THE TREATMENT OF SPINAL MUSCULAR ATROPHY