(19)
(11) EP 3 790 545 A1

(12)

(43) Date of publication:
17.03.2021 Bulletin 2021/11

(21) Application number: 19742516.8

(22) Date of filing: 17.07.2019
(51) International Patent Classification (IPC): 
A61K 31/365(2006.01)
A61K 45/06(2006.01)
A61K 31/551(2006.01)
(86) International application number:
PCT/US2019/000033
(87) International publication number:
WO 2021/010937 (21.01.2021 Gazette 2021/03)
(84) Designated Contracting States:
AL AT BE BG CH CY CZ DE DK EE ES FI FR GB GR HR HU IE IS IT LI LT LU LV MC MK MT NL NO PL PT RO RS SE SI SK SM TR
Designated Extension States:
BA ME
Designated Validation States:
KH MA MD TN

(71) Applicant: EMMAUS MEDICAL, INC.
Torrance CA 90503 (US)

(72) Inventor:
  • NIIHARA, Yutaka
    Rolling Hills Estates CA 90274 (US)

(74) Representative: Boult Wade Tennant LLP 
Salisbury Square House 8 Salisbury Square
London EC4Y 8AP
London EC4Y 8AP (GB)

   


(54) METHODS AND COMPOSITIONS FOR THE TREATMENT OF SICKLE CELL DISEASES AND THALASSEMIA