(19)
(11) EP 3 946 467 A1

(12)

(43) Date of publication:
09.02.2022 Bulletin 2022/06

(21) Application number: 20723243.0

(22) Date of filing: 02.04.2020
(51) International Patent Classification (IPC): 
A61K 48/00(2006.01)
C12N 15/864(2006.01)
(52) Cooperative Patent Classification (CPC):
C07K 2317/41; A61P 27/02; C12N 15/86; C12N 2750/14143; A61K 2039/54; C07K 2317/55; A61K 2039/53; C12N 2799/04; C07K 16/22; C07K 2317/567; C07K 2317/522; C07K 2317/76; A61K 48/0075; C07K 2317/24; C07K 2317/515
(86) International application number:
PCT/US2020/026356
(87) International publication number:
WO 2020/206098 (08.10.2020 Gazette 2020/41)
(84) Designated Contracting States:
AL AT BE BG CH CY CZ DE DK EE ES FI FR GB GR HR HU IE IS IT LI LT LU LV MC MK MT NL NO PL PT RO RS SE SI SK SM TR
Designated Extension States:
BA ME
Designated Validation States:
KH MA MD TN

(30) Priority: 03.04.2019 US 201962828949 P
03.06.2019 US 201962856533 P
10.12.2019 US 201962946158 P

(71) Applicant: REGENXBIO Inc.
Rockville, MD 20850 (US)

(72) Inventors:
  • DANOS, Olivier
    New York, NY 10128 (US)
  • VAN EVEREN, Sherri
    Menlo Park, CA 94025 (US)
  • YOO, Jesse, I.
    Atlanta, GA 30307 (US)
  • PATEL, Samir, Maganbhai
    Washington, DC 20009 (US)
  • GHANEKAR, Avanti, Arvind
    St. Louis, MO 63018 (US)
  • O'BERRY, Anthony, Ray
    Clarksburg, MD 20871 (US)
  • IRWIN-PACK, Kim, Rees
    Milcreek, UT 84109 (US)
  • CURTISS, Darin, Thomas
    Potomac, MD 20854 (US)

(74) Representative: Jones Day 
Rechtsanwälte, Attorneys-at-Law, Patentanwälte Prinzregentenstrasse 11
80538 München
80538 München (DE)

   


(54) GENE THERAPY FOR EYE PATHOLOGIES