(19)
(11) EP 4 288 441 A1

(12)

(43) Date of publication:
13.12.2023 Bulletin 2023/50

(21) Application number: 22750319.0

(22) Date of filing: 02.02.2022
(51) International Patent Classification (IPC): 
C07D 487/04(2006.01)
(52) Cooperative Patent Classification (CPC):
C07D 487/04; A61K 31/519
(86) International application number:
PCT/US2022/014929
(87) International publication number:
WO 2022/169864 (11.08.2022 Gazette 2022/32)
(84) Designated Contracting States:
AL AT BE BG CH CY CZ DE DK EE ES FI FR GB GR HR HU IE IS IT LI LT LU LV MC MK MT NL NO PL PT RO RS SE SI SK SM TR
Designated Extension States:
BA ME
Designated Validation States:
KH MA MD TN

(30) Priority: 05.02.2021 US 202163146139 P

(71) Applicant: PTC Therapeutics, Inc.
South Plainfield, NJ 07080 (US)

(72) Inventors:
  • ARACHCHILAGE, Gayan Mirihana
    Plainfield, New Jersey 07080 (US)
  • ARNOLD, Michael A.
    Plainfield, New Jersey 07080 (US)
  • BARRAZA, Scott
    Plainfield, New Jersey 07080 (US)
  • BHATTACHARYYA, Anuradha
    Plainfield, New Jersey 07080 (US)
  • KARP, Gary Mitchell
    Plainfield, New Jersey 07080 (US)

(74) Representative: Dennemeyer & Associates S.A. 
Postfach 70 04 25
81304 München
81304 München (DE)

   


(54) METHODS FOR TREATING SPINOCEREBELLAR ATAXIA TYPE 3