(19)
(11) EP 4 568 962 A2

(12)

(88) Date of publication A3:
28.03.2024

(43) Date of publication:
18.06.2025 Bulletin 2025/25

(21) Application number: 23853472.1

(22) Date of filing: 08.08.2023
(51) International Patent Classification (IPC): 
C07D 419/14(2006.01)
A61P 43/00(2006.01)
A61K 31/4365(2006.01)
(52) Cooperative Patent Classification (CPC):
A61K 31/4365
(86) International application number:
PCT/US2023/071833
(87) International publication number:
WO 2024/036143 (15.02.2024 Gazette 2024/07)
(84) Designated Contracting States:
AL AT BE BG CH CY CZ DE DK EE ES FI FR GB GR HR HU IE IS IT LI LT LU LV MC ME MK MT NL NO PL PT RO RS SE SI SK SM TR
Designated Extension States:
BA
Designated Validation States:
KH MA MD TN

(30) Priority: 09.08.2022 US 202263370902 P

(71) Applicant: PTC Therapeutics, Inc.
Warren, NJ 07059 (US)

(72) Inventor:
  • LI, Wencheng
    Plainfield, New Jersey 07080 (US)

(74) Representative: Nederlandsch Octrooibureau 
P.O. Box 29720
2502 LS The Hague
2502 LS The Hague (NL)

   


(54) METHODS FOR MODULATING RNA SPLICING