(19)
(11) EP 4 771 151 A2

(12)

(88) Date of publication A3:
01.05.2025

(43) Date of publication:
08.07.2026 Bulletin 2026/28

(21) Application number: 24861232.7

(22) Date of filing: 30.08.2024
(51) International Patent Classification (IPC): 
C12N 15/11(2006.01)
A61K 31/711(2006.01)
(52) Cooperative Patent Classification (CPC):
A61K 31/711; A61K 31/713; C12N 2310/14; C12N 15/113; C12N 2310/141; C12N 2310/3515; A61K 47/542
(86) International application number:
PCT/US2024/044874
(87) International publication number:
WO 2025/050048 (06.03.2025 Gazette 2025/10)
(84) Designated Contracting States:
AL AT BE BG CH CY CZ DE DK EE ES FI FR GB GR HR HU IE IS IT LI LT LU LV MC ME MK MT NL NO PL PT RO RS SE SI SK SM TR
Designated Extension States:
BA
Designated Validation States:
GE KH MA MD TN

(30) Priority: 31.08.2023 US 202363579888 P
22.12.2023 US 202363614364 P

(71) Applicant: Iris Medicine, Inc.
Berkeley, California 94704 (US)

(72) Inventors:
  • HOLTER, Joshua Nelson
    Berkeley, California 94704 (US)
  • LEE, Lorene Lai Ying
    Berkeley, California 94704 (US)

(74) Representative: Elkington and Fife LLP 
Prospect House 8 Pembroke Road
Sevenoaks, Kent TN13 1XR
Sevenoaks, Kent TN13 1XR (GB)

   


(54) METHODS AND COMPOSITIONS FOR TREATING GGGGCC REPEAT EXPANSION DISEASES